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ABOUT US
OVERVIEW
MILESTONES
LEADERSHIP
INVESTORS
SCIENCE & TECHNOLOGY PLATFORM
PIPELINE
PRESS RELEASE
CONTACT US
Accurate Editing for Cures
Delivering the best in vivo gene editing medicine
May 12, 2025
AccurEdit Therapeutics to present at the 2025 Annual Meeting of the American Society of Gene & Cell Therapy
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Positively Transforming Patient's Life with Genome Editing
BREAKING THE GROUND FOR PATIENTS IN NEED
First in China: safe and effective systemic CRISPR gene editing in humans
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Proven capability and track record to deliver innovative products in China and the US in industry-leading speed
PRODUCT WITH AN EDGE
Potentially best-in-class in vivo gene editing product for ATTR
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> 90% serum TTR reduction after 4 weeks
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No off target editing detected at up to ~80 times of EC90
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No infusion-related reaction observed
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No > Grade 1 liver enzyme elevation observed
PLATFORM THAT PERFORMS
Industry-leading end-to-end in vivo gene editing platform
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RNA synthesis (Research and GMP grade)
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Editing (Patented base editors and Cas enzymes; industry-leading capability of gRNA screening and optimization)
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Delivery (Industry-leading efficiency and specificity)
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